Kilpatrick Townsend & Stockton LLP
Small molecule inhibitors targeting CAG-repeat RNA toxicity in polyglutamine diseases
The present invention provides for a novel method for treating polyglutamine (polyQ) diseases. Also disclosed are related compositions and kits for therapeutic use in the treatment of polyQ diseases.
The Chinese University of Hong Kong
A H
A61K H05K
inventional additional
Qian Ho Yin Edwin Shaohong Jacky Chi-Ki Chun-Ho
Zhang Chan Peng Ngo Wong