Parker Highlander PLLC
Methods and compounds useful in conditions related to repeat expansion
Described are compounds and methods useful for the treatment and investigation of diseases and disorders associated with expanded repeat-containing RNA molecules. In certain embodiments, compounds and methods useful for the modulation of ATXN-3 pre-mRNA are described. In certain embodiments, compounds and methods useful for the modulation of ATN-1 mRNA are described.
IONIS PHARMACEUTICALS, INC. THE BOARD OF REGENTS OF THE UNIVERSITY OF TEXAS SYSTEM
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Jing Eric E. David Dongbo Jiaxin Thazha P.
Liu Swayze Corey Yu Hu Prakash